Orphan drug under study to be available to more patients

Article

Gentium expands access to defibrotide under compassionate use basis

Gentium S.p.A has announced that it is expanding access to its investigational drug defibrotide for patients to treat severe veno-occlusive disease (VOD). The Villa Guardia, Italy, firm is taking this step because it has received "large numbers of requests" for the drug on a compassionate use basis. Gentium added that the expanded access will not affect the Phase III trial of the drug, since only patients who are not eligible to, or cannot, participate in the study can take advantage of the expanded access program. Defibrotide is an orphan drug that has been granted fast-track designation to treat severe VOD in stem cell transplant patients.

To see more Daily News articles, click here.

To go to the Drug Topics homepage, click here.

 

Recent Videos
fake news misinformation | Image Credit: Bits and Splits - stock.adobe.com
© 2024 MJH Life Sciences

All rights reserved.